Kevin Flanigan

Director, Center for Gene Therapy · Nationwide Children's Hospital · company speakers →

Dr. Flanigan is the Director of The Center for Gene Therapy at Nationwide Children's Hospital in Columbus, Ohio, where he holds the Robert F. & Edgar T. Wolfe Foundation Endowed Chair in Neuromuscular Research. He directs the NCH Neuromuscular Program as well as Nationwide Children's NICHD P50-funded Muscular Dystrophy Specialized Research Center. He trained in Neurology & Neuromuscular Medicine at Johns Hopkins University, pursued a post-doctoral fellowship in Human Molecular Biology and Genetics at the University of Utah, and currently holds appointments as Professor of Pediatrics and Neurology at the Ohio State University.<br><br>His laboratory research focuses on genotype/phenotype correlations in the muscular dystrophies, with a goal of understanding molecular mechanisms that lead to amelioration of symptoms in order to identify new therapeutic pathways. His lab works primarily on AAV-based approaches to gene therapy, including viral-vector based exon skipping, gene editing, and gene replacement. An experienced clinical trialist, he initiated INDs for trials of gene replacement in Sanfilippo syndrome types A and B, for which he still serves as a principal investigator. <br>

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